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      A.24 Risdiplam – spinal muscular atrophy

      Application, expert reviews and public comments

      Application

      A.24 Risdiplam – spinal muscular atrophy

      A.24 Risdiplam - update from the applicant (2 April 2025)

      Expert reviews

      Expert Review 1

      Expert Review 2

      Comments

      WHO Department Comments

      Patient groups and healthcare professionals

      Richard Finkel

      Mental Health, Brain Health, and Substance Use

      Maternal, Newborn, Child and Adolescent Health and Ageing

       

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